Research
Since 1984, we’ve invested $75 million in the research that has made today’s breakthroughs possible. We advance a comprehensive research program, attacking SMA from all sides.
Our Strategy
Our approach includes four research areas—basic research, drug discovery, clinical trials, and clinical care—working together toward our vision of a world without SMA. READ MORE
Latest Advances
Read more about the SMA drug pipeline and other major developments in research. READ MORE
For Researchers
Researchers can apply for funding opportunities, attend the SMA Research Group Meeting, or request assistance in recruiting for clinical trials. READ MORE
Research Publications
Browse past issues of Compass, our quarterly research newsletter, and other relevant publications. READ MORE